Plenary & Themed Session 5: Therapies
Tuesday, August 6, 2019 |
8:30 AM - 10:00 AM |
Auditorium (L1) |
Details
Chairs: Dr Emma Glamuzina & A/Prof Kathy Tucker
Speaker
Prof Peter Clayton
Professor of Paediatric Metabolic Disease and Hepatology
Institute of Child Health UCL
ASSESSING THE EFFECTS OF NEW SMALL MOLECULE-BASED TREATMENTS
8:30 AM - 8:55 AM
Dr Edward Wild
Consultant Neurologist
National Hospital for Neurology and Neurosurgery
ANTISENSE HUNTINGTIN-LOWERING DRUGS FOR HUNTINGTON’S DISEASE: WHERE ARE WE NOW, AND WHAT’S NEXT?
8:55 AM - 9:20 AM
Prof Ravi Savarirayan
Consultant
Murdoch Children's Research Institute
DRUG TRIALS IN SKELETAL DYSPLASIA
9:20 AM - 9:40 AM
Professor John Christodoulou
Director, Genomic Medicine Research Theme
Murdoch Children's Research Institute
THERAPEUTIC ADVANCES IN THE MANAGEMENT OF MITOCHONDRIAL DISORDERS
9:40 AM - 10:00 AM