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Plenary & Themed Session 5: Therapies

Tuesday, August 6, 2019
8:30 AM - 10:00 AM
Auditorium (L1)

Details

Chairs: Dr Emma Glamuzina & A/Prof Kathy Tucker


Speaker

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Prof Peter Clayton
Professor of Paediatric Metabolic Disease and Hepatology
Institute of Child Health UCL

ASSESSING THE EFFECTS OF NEW SMALL MOLECULE-BASED TREATMENTS

8:30 AM - 8:55 AM
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Dr Edward Wild
Consultant Neurologist
National Hospital for Neurology and Neurosurgery

ANTISENSE HUNTINGTIN-LOWERING DRUGS FOR HUNTINGTON’S DISEASE: WHERE ARE WE NOW, AND WHAT’S NEXT?

8:55 AM - 9:20 AM
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Prof Ravi Savarirayan
Consultant
Murdoch Children's Research Institute

DRUG TRIALS IN SKELETAL DYSPLASIA

9:20 AM - 9:40 AM
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Professor John Christodoulou
Director, Genomic Medicine Research Theme
Murdoch Children's Research Institute

THERAPEUTIC ADVANCES IN THE MANAGEMENT OF MITOCHONDRIAL DISORDERS

9:40 AM - 10:00 AM
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